NHS Approves £2.6M Hemgenix Gene Therapy for Haemophilia B, Promising Decade-Long Relief

June 28, 2024
NHS Approves £2.6M Hemgenix Gene Therapy for Haemophilia B, Promising Decade-Long Relief
  • CSL Behring's Hemgenix gene therapy for haemophilia B has received NHS approval in the UK.

  • NICE has granted coverage for adults with severe or moderately severe haemophilia B.

  • Denmark has recommended reimbursement for Hemgenix, the first Nordic country to do so.

  • The therapy costs £2.6 million per patient and is described as potentially 'transformative'.

  • Hemgenix aims to correct FIX deficiency and reduce the need for frequent replacement therapies.

  • Trial patients have reported staying off injections for years, with some feeling 'cured'.

  • The one-shot infusion therapy could last up to a decade.

  • The NHS will offer Hemgenix for free to around 250 eligible patients in England.

  • Around 260 out of 2,000 haemophilia B patients in the UK could benefit.

  • The Haemophilia Society has praised the potential of gene therapy to enhance quality of life.

  • Experts believe Hemgenix could save the NHS money by reducing the need for expensive treatments and surgeries.

  • The rollout marks a significant step in evaluating cell and gene therapies in the UK.

  • An outcomes-based payment model is being used for the first time.

  • NHS England is encouraging eligible patients to discuss Hemgenix with their healthcare professionals.

Summary based on 5 sources


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