18-Month-Old Becomes Youngest to Regain Hearing with Gene Therapy Breakthrough

May 10, 2024
18-Month-Old Becomes Youngest to Regain Hearing with Gene Therapy Breakthrough
  • 18-month-old Opal Sandy becomes youngest to regain hearing via gene therapy trial by Regeneron.

  • The therapy corrects a rare genetic mutation linked to hereditary deafness, with Opal's hearing near normal.

  • A working copy of the OTOF gene is delivered to patients to rectify auditory neuropathy.

  • This medical advancement signals a new chapter in treating genetic hearing impairments.

  • The ongoing trial spans the UK, Spain, and the US, aiming to potentially cure genetic deafness in up to 18 children.

  • Opal's case sparks hope for future treatments that could benefit a wider population with similar conditions.

  • Adapting to Opal's recovery, her parents now embrace her eagerness to explore sounds.

Summary based on 6 sources


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