18-Month-Old Becomes Youngest to Regain Hearing with Gene Therapy Breakthrough
May 10, 202418-month-old Opal Sandy becomes youngest to regain hearing via gene therapy trial by Regeneron.
The therapy corrects a rare genetic mutation linked to hereditary deafness, with Opal's hearing near normal.
A working copy of the OTOF gene is delivered to patients to rectify auditory neuropathy.
This medical advancement signals a new chapter in treating genetic hearing impairments.
The ongoing trial spans the UK, Spain, and the US, aiming to potentially cure genetic deafness in up to 18 children.
Opal's case sparks hope for future treatments that could benefit a wider population with similar conditions.
Adapting to Opal's recovery, her parents now embrace her eagerness to explore sounds.
Summary based on 6 sources
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Sources
The Guardian • May 9, 2024
UK toddler has hearing restored in world first gene therapy trialMedical Xpress • May 9, 2024
UK girl's hearing restored after groundbreaking gene therapyGround News • May 9, 2024
Toddler born deaf can hear after world-first gene therapy