GenSight Unveils Breakthrough LHON Gene Therapy Data at Neuro-Ophthalmology Meeting

March 4, 2024
GenSight Unveils Breakthrough LHON Gene Therapy Data at Neuro-Ophthalmology Meeting
  • GenSight Biologics is set to present new data on LUMEVOQ®, their gene therapy for LHON, at the 50th Annual Meeting of the North American Neuro-Ophthalmology Society.

  • The company will share evidence of LUMEVOQ®'s efficacy, including success in transfecting retinal ganglion cells, improving visual acuity, and offering better visual recovery than other treatments.

  • Analyses will highlight LUMEVOQ®'s impact on patients' quality of life and compare its effectiveness with natural LHON progression and idebenone treatment.

  • The European Medicines Agency has recognized LUMEVOQ® as the invented name for GenSight's lead product candidate GS010, which is currently in Phase III trials.

  • GS010 targets Leber's Hereditary Optic Neuropathy (LHON), a rare genetic disorder causing blindness, with a focus on teens and young adults.

  • For additional information, inquiries can be directed to GenSight's CFO Ivan Tortet or LifeSci Advisors' Investor Relations representative Guillaume van Renterghem.

Summary based on 2 sources


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